Rare Zebra

Rare disease search prototype built on Orphanet data

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ORPHA:351

Galactosialidosis

Also called Goldberg syndrome, Neuraminidase deficiency with beta-galactosidase deficiency

Body system
Bone diseases
Inheritance pattern
Autosomal recessive
Typical age of onset
All ages
Estimated prevalence
Unknown (Worldwide)
Rarity class
Unknown

ORPHA:351 is classified under "Bone diseases" in the Orphanet nomenclature.

Common signs

  • Coarse facial features
  • Hearing impairment
  • Abnormality of the vertebral column
  • Intellectual disability
  • Seizure
  • Skeletal dysplasia