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Rare disease search prototype built on Orphanet data

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ORPHA:183678

Hermansky-Pudlak syndrome due to AP-3 deficiency

Also called Hermansky-Pudlak syndrome due to adaptor protein 3 complex deficiency, Hermansky-Pudlak syndrome with neutropenia

Body system
Inborn errors of metabolism
Inheritance pattern
Autosomal recessive
Typical age of onset
Neonatal
Estimated prevalence
<1 / 1 000 000 (Worldwide)
Rarity class
<1 / 1 000 000

ORPHA:183678 is classified under "Inborn errors of metabolism" in the Orphanet nomenclature.

Common signs